Unmet Medical Needs in Pediatric Endocrinology

Pediatric endocrinology has made remarkable advances over recent decades, transforming the lives of countless children and families. Yet, major challenges persist. Many rare and complex endocrine disorders remain difficult to diagnose, monitor, and treat effectively. Disparities in access to specialized care, limited research investment, and fragmented health systems continue to create inequities in outcomes across regions and populations. This document arises from the collective effort of the European Society for Paediatric Endocrinology (ESPE) to highlight these unmet medical needs and to chart a path forward. It underscores the necessity of harmonized diagnostic standards, innovative research, and sustainable policies that support both patients and professionals. By identifying key barriers and proposing strategic directions, ESPE aims to foster collaboration among clinicians, researchers, policymakers, and patient communities. Only through coordinated action can we ensure that every child with an endocrine disorder receives equitable, timely, and high-quality care-regardless of where they live.