We describe a case of acute myeloid leukemia with NPM1 mutation and disseminated leukemia cutis in a very old patient, who achieved a long-lasting response to the azacitidine/venetoclax combination with molecular complete remission, given the potential value of this rarely observed clinical outcome.

Niscola, P., Mazzone, C., Fratoni, S., Ardu, N.r., Cesini, L., Giovannini, M., et al. (2023). Acute myeloid leukemia with NPM1 mutation and disseminated leukaemia cutis: achievement of molecular complete remission by venetoclax/azacytidine combination in a very old patient. ACTA HAEMATOLOGICA, 1 [10.1159/000531101].

Acute myeloid leukemia with NPM1 mutation and disseminated leukaemia cutis: achievement of molecular complete remission by venetoclax/azacytidine combination in a very old patient

Mazzone, Carla;Giovannini, Marco;Ottone, Tiziana;Anemona, Lucia;Voso, Maria Teresa;de Fabritiis, Paolo
2023-05-17

Abstract

We describe a case of acute myeloid leukemia with NPM1 mutation and disseminated leukemia cutis in a very old patient, who achieved a long-lasting response to the azacitidine/venetoclax combination with molecular complete remission, given the potential value of this rarely observed clinical outcome.
17-mag-2023
Pubblicato
Rilevanza internazionale
Articolo
Esperti anonimi
Settore MED/15 - MALATTIE DEL SANGUE
English
Acute myeloid leukemia
Leukemia cutis
Nucleophosmin-1
Venetoclax
azacitidine
Niscola, P., Mazzone, C., Fratoni, S., Ardu, N.r., Cesini, L., Giovannini, M., et al. (2023). Acute myeloid leukemia with NPM1 mutation and disseminated leukaemia cutis: achievement of molecular complete remission by venetoclax/azacytidine combination in a very old patient. ACTA HAEMATOLOGICA, 1 [10.1159/000531101].
Niscola, P; Mazzone, C; Fratoni, S; Ardu, Nr; Cesini, L; Giovannini, M; Ottone, T; Anemona, L; Voso, Mt; de Fabritiis, P
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Utilizza questo identificativo per citare o creare un link a questo documento: https://hdl.handle.net/2108/329223
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